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sma spinal muscular atrophy zolgensma in utero fetal gene therapy smn1
Fetal Gene Therapy Helps Mice with Spinal Muscular Atrophy
The animals lived longer and showed milder symptoms than untreated mice, although they didn’t survive as long as wildtype mice.
Fetal Gene Therapy Helps Mice with Spinal Muscular Atrophy
Fetal Gene Therapy Helps Mice with Spinal Muscular Atrophy

The animals lived longer and showed milder symptoms than untreated mice, although they didn’t survive as long as wildtype mice.

The animals lived longer and showed milder symptoms than untreated mice, although they didn’t survive as long as wildtype mice.

rare diseases, disease & medicine, genetics & genomics

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