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rare diseases, cell & molecular biology

Infographic: Piecing the Cholesterol Puzzle
Diana Kwon | Apr 30, 2018 | 1 min read
How a rare disease led to an understanding of the basics of cholesterol regulation.
Gene Therapy Coming of Age?
Dan Cossins | Jul 11, 2013 | 4 min read
Using lentiviral vectors to replace mutated genes in blood stem cells, scientists successfully treat two rare diseases apparently without causing harmful side effects.
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