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image: Positive Trial Results for Experimental DMD Gene Therapy

Positive Trial Results for Experimental DMD Gene Therapy

By Catherine Offord | June 20, 2018

Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.

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image: Dopamine Neuron Implants Ease Parkinson’s Symptoms in Monkeys

Dopamine Neuron Implants Ease Parkinson’s Symptoms in Monkeys

By Sukanya Charuchandra | June 20, 2018

The stem cell–derived transplants were stable for 24 months and led to wide-ranging behavioral improvements in the monkeys.  

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image: Cell Transplant Trial for Spinal Injury Is Safe

Cell Transplant Trial for Spinal Injury Is Safe

By Ruth Williams | June 1, 2018

The first human experiment with neural precursor cells implanted to treat chronic spinal cord injury suggests the procedure is safe, and hints at a small benefit.  

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Understanding the factors that influence spillover could help forecast future epidemics.  

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image: Predicting Future Zoonotic Disease Outbreaks

Predicting Future Zoonotic Disease Outbreaks

By Ashley Yeager | June 1, 2018

A step-by-step study of diseases that jump species gives subtle clues about future epidemics.

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Doctors treated the fetus, who has alpha thalassemia major, with cells from her mother’s bone marrow.

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Biotechs have developed enzyme replacements and genetically modified probiotics to treat patients with the rare metabolic disorder.

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image: Image of the Day: Jasper the Cat

Image of the Day: Jasper the Cat

By The Scientist Staff | May 22, 2018

Researchers found a previously undiscovered hepadnavirus in an immunocompromised cat.

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image: Image of the Day: Hammerhead

Image of the Day: Hammerhead

By The Scientist Staff | May 21, 2018

This hammer-headed fruit bat is wearing a GPS tracker deployed by researchers with the Wildlife Conservation Society.

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As the first personalized cell and gene therapies are approved from small clinical trials, researchers propose the creation of publicly accessible databases to pull together real-world results.  

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