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Sangamo Therapeutics will use zinc finger nucleases to introduce the gene for a missing clotting factor into the livers of men with hemophilia B.

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image: Targeting DNA

Targeting DNA

By | June 1, 2012

After 20 years of high-profile failure, gene therapy is finally well on its way to clinical approval.

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image: Gene Editing Treats Blood Disease

Gene Editing Treats Blood Disease

By | June 27, 2011

Revising a dysfunctional gene in vivo for the first time, researchers successfully restore blood clotting in hemophiliac mice.

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