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Trial of Gene Therapy for Duchenne Muscular Dystrophy Put on Hold
Trial of Gene Therapy for Duchenne Muscular Dystrophy Put on Hold
The US Food and Drug Administration halts a study by Solid Biosciences after a patient experiences severe side effects following treatment.
The US Food and Drug Administration halts a study by Solid Biosciences after a patient experiences severe side effects following treatment.
genetics & genomics, drug development, clinical trials, disease & medicine
Recent Trials for Fragile X Syndrome Offer Hope
Randi Hagerman | Sep 1, 2019 | 10+ min read
Despite a solid understanding of the biological basis of fragile X syndrome, researchers have struggled to develop effective treatments.