WORTH WAITING FOR: Kwaku Ohene-Frempong of the Sickle Cell Disease Association of America says "gene therapy is the ultimate cure of sickle cell disease."
Within the last two years, several treatments have been developed that attack the cause and the significant symptoms of the disease. Bone-marrow transplantation can now provide a true cure for a small percentage of people with sickle cell disease. Two animal models have been developed. And researchers harbor realistic hopes that genetic therapy could actually cure the majority of sufferers.