drug development

From Concept to Cure: Using AAV in Gene Therapy

With the right tools and techniques, researchers develop safe and effective adeno-associated virus (AAV)-based gene therapies.

Because viruses efficiently insert nucleic acids into host cells upon infection, they are attractive vehicles for gene delivery. In the past, many viral gene delivery agents were unsuitable for clinical applications due to their high immunogenicity and propensity to cause cancer. To bring gene therapy to the clinic, scientists now use adeno-associated viruses (AAVs) for safe and effective gene delivery.

Download this ebook from Bio-Rad to learn about

  • Techniques for developing safe and effective AAV vectors for gene therapy
  • Characterizing AAVs during production
  • AAV-based gene therapy success stories

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