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FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease
The medicine increases the activity of a deficient enzyme in certain patients with the condition.
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

epigenetics, disease & medicine, immunology, genetics & genomics
First RNAi Therapy Approved by FDA
First RNAi Therapy Approved by FDA
Kerry Grens | Aug 10, 2018
Alnylam’s patisiran interferes with the production of a mutated protein present in people with hereditary transthyretin amyloidosis.
Doubts Arise Again About CRISPR’d Human EmbryosDoubts Arise Again About CRISPR’d Human Embryos
Doubts Arise Again About CRISPR’d Human Embryos
Kerry Grens | Aug 8, 2018
One lab finds that a similar method produces large genetic deletions when performed in mouse embryos.
Former Congresswoman, HHS Secretary Margaret Heckler Dies
Former Congresswoman, HHS Secretary Margaret Heckler Dies
Catherine Offord | Aug 7, 2018
Appointed by Ronald Reagan, Heckler led the agency from 1983 to 1985, and helped promote research into AIDS.
Zika’s Effects on Babies Can Show Up Later
Zika’s Effects on Babies Can Show Up Later
Kerry Grens | Aug 7, 2018
The CDC finds one in seven children exposed to the virus in utero experiences health problems by age one.
Invasive Tick Species Spreads in Eastern US
Invasive Tick Species Spreads in Eastern US
Shawna Williams | Aug 7, 2018
The Asian longhorned tick, first found in the country last year, is now present in several states.
Experimental Ebola Vaccinations to Resume in Democratic Republic of Congo
Experimental Ebola Vaccinations to Resume in Democratic Republic of Congo
Ashley Yeager | Aug 6, 2018
In response to a new outbreak, health workers will start administering vaccines again soon.
Lab-Grown Lungs Transplanted into Pigs
Lab-Grown Lungs Transplanted into Pigs
Sukanya Charuchandra | Aug 3, 2018
The lungs survived with no complications in the animals for up to two months.
Language Gene Dethroned
Language Gene Dethroned
Shawna Williams | Aug 3, 2018
Contrary to earlier results, FOXP2 did not undergo a “selective sweep” as humans developed language, a study finds.
Novartis and Sanofi Stockpile Meds in Preparation for Brexit
Novartis and Sanofi Stockpile Meds in Preparation for Brexit
Ashley Yeager | Aug 3, 2018
If the UK leaves the EU in March without a deal, transport of insulin and other essential drugs could be delayed.