Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging
Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.
Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging

Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.

Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.

marine biology, disease & medicine, immunology, genetics & genomics
Image of the Day: Ocean Wonder
Image of the Day: Ocean Wonder
Sukanya Charuchandra | Sep 4, 2018
Molecules similar to those produced by sea anemones are neuroprotective in a mouse cell model of Alzheimer’s disease.
US Companies Launch CRISPR Clinical Trial
US Companies Launch CRISPR Clinical Trial
Catherine Offord | Sep 3, 2018
The Germany-based study will test an ex vivo genome-editing therapy for the inherited blood disorder β-thalassemia.
Old Age Has Links to Redox Stress in Muscles
Old Age Has Links to Redox Stress in Muscles
Sukanya Charuchandra | Sep 1, 2018
Even if people exercise, hydrogen peroxide and other reactive molecules continue to accumulate in the tissues.
Putting Exosomes to Work
Putting Exosomes to Work
Ruth Williams | Sep 1, 2018
Researchers identify a handy tool for tinkering with the versatile vesicles.
Infographic: Red Blood Cell Shape
Infographic: Red Blood Cell Shape
Ashley Yeager | Sep 1, 2018
What happens when myosin inside red blood cells can't do its job?
Soft Robotics Find a Place in the OceanSoft Robotics Find a Place in the Ocean
Soft Robotics Find a Place in the Ocean
Sukanya Charuchandra | Sep 1, 2018
Scientists who designed a marine robot to survey ocean life were inspired by eel larvae.
Vibrations Restore Sense of Movement in Prosthetics
Vibrations Restore Sense of Movement in Prosthetics
Diana Kwon | Sep 1, 2018
Scientists recreate proprioception for people with artificial arms using a perceptual illusion.
Infographic: Directing Exosome Traffic
Infographic: Directing Exosome Traffic
Ruth Williams | Sep 1, 2018
Researchers harness a protein to send cargo-carrying exosomes to mouse muscles.
CRISPR Treatment for Duchenne Muscular Dystrophy Helps Dogs
CRISPR Treatment for Duchenne Muscular Dystrophy Helps Dogs
Catherine Offord | Aug 31, 2018
Researchers boosted levels of the dystrophin protein to nearly normal levels in a canine model of the disease.