ISTOCK, D3DAMON
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease
The medicine increases the activity of a deficient enzyme in certain patients with the condition.
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

policy, genetics & genomics, disease & medicine
First RNAi Therapy Approved by FDA
First RNAi Therapy Approved by FDA
Kerry Grens | Aug 10, 2018
Alnylam’s patisiran interferes with the production of a mutated protein present in people with hereditary transthyretin amyloidosis.
Doubts Arise Again About CRISPR’d Human EmbryosDoubts Arise Again About CRISPR’d Human Embryos
Doubts Arise Again About CRISPR’d Human Embryos
Kerry Grens | Aug 8, 2018
One lab finds that a similar method produces large genetic deletions when performed in mouse embryos.
Salk Institute Settles Two Gender Discrimination Suits
Salk Institute Settles Two Gender Discrimination Suits
Sukanya Charuchandra | Aug 8, 2018
A third case against the biomedical institute will be heard in court.
Wild Cat Conservationist Alan Rabinowitz Dies
Wild Cat Conservationist Alan Rabinowitz Dies
Ashley Yeager | Aug 8, 2018
The “Indiana Jones of Wildlife Protection” helped established nature preserves around the world.
Former Congresswoman, HHS Secretary Margaret Heckler Dies
Former Congresswoman, HHS Secretary Margaret Heckler Dies
Catherine Offord | Aug 7, 2018
Appointed by Ronald Reagan, Heckler led the agency from 1983 to 1985, and helped promote research into AIDS.
Zika’s Effects on Babies Can Show Up Later
Zika’s Effects on Babies Can Show Up Later
Kerry Grens | Aug 7, 2018
The CDC finds one in seven children exposed to the virus in utero experiences health problems by age one.
Invasive Tick Species Spreads in Eastern US
Invasive Tick Species Spreads in Eastern US
Shawna Williams | Aug 7, 2018
The Asian longhorned tick, first found in the country last year, is now present in several states.
Q&A: Scientist and Advocate BethAnn McLaughlinQ&A: Scientist and Advocate BethAnn McLaughlinQ&A: Scientist and Advocate BethAnn McLaughlinQ&A: Scientist and Advocate BethAnn McLaughlin
Q&A: Scientist and Advocate BethAnn McLaughlin
Anna Azvolinsky | Aug 7, 2018
The neuroscientist talks about her experiences with trying to change how the scientific community copes with sexual assault and harassment.
Experimental Ebola Vaccinations to Resume in Democratic Republic of Congo
Experimental Ebola Vaccinations to Resume in Democratic Republic of Congo
Ashley Yeager | Aug 6, 2018
In response to a new outbreak, health workers will start administering vaccines again soon.