ISTOCK, D3DAMON
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease
The medicine increases the activity of a deficient enzyme in certain patients with the condition.
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

The medicine increases the activity of a deficient enzyme in certain patients with the condition.

rare diseases, culture
First RNAi Therapy Approved by FDA
First RNAi Therapy Approved by FDA
Kerry Grens | Aug 10, 2018
Alnylam’s patisiran interferes with the production of a mutated protein present in people with hereditary transthyretin amyloidosis.
Officially Intelligent
Officially Intelligent
Bob Grant | Aug 1, 2018
Humanity is on the precipice of major change. Some fear a world ruled by bots. I fear a world ruled by people.
Lessons from Biosphere 2
Lessons from Biosphere 2
Mark Nelson | Aug 1, 2018
Both the scientific community and the general public still have a lot to learn from the largest mesocosm research project ever conducted.
Image of the Day: Blooming Algae
Image of the Day: Blooming Algae
Sukanya Charuchandra | Jul 9, 2018
The British Phycological Society declares the winners of a photography contest for images of algae.
Two University of Rochester Professors Resign in Protest
Two University of Rochester Professors Resign in Protest
Sukanya Charuchandra | Jun 20, 2018
Celeste Kidd and Steven Piantadosi had sued the university over its handling of sexual harassment allegations made against colleague Florian Jaeger.
Positive Trial Results for Experimental DMD Gene Therapy
Positive Trial Results for Experimental DMD Gene Therapy
Catherine Offord | Jun 20, 2018
Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.
Prominent Salk Institute Scientist Inder Verma Resigns
Prominent Salk Institute Scientist Inder Verma Resigns
Sukanya Charuchandra | Jun 12, 2018
His decision came as an investigation into sexual harassment allegations against him was ongoing.  
Ten-Minute Sabbatical
Ten-Minute Sabbatical
The Scientist Staff | Jun 1, 2018
Take a break from the bench to puzzle and peruse.
In Utero Transplant in First Clinical Trial Successful
In Utero Transplant in First Clinical Trial Successful
Jim Daley | May 30, 2018
Doctors treated the fetus, who has alpha thalassemia major, with cells from her mother’s bone marrow.