Canavan disease
Families of Children with Rare Diseases Fuel Gene Therapy Research
The Scientist Staff | May 1, 2018 | 10+ min read
Crowdfunding can power investigations into diseases that would otherwise receive little attention.
Slow March Toward a Canavan Cure
Ashley Yeager | May 1, 2018 | 5 min read
Two decades after a successful crowdfunding campaign, some clinical trial patients have seen improvements—but there’s still no approved treatment for the disease.
Fighting Canavan Disease
The Scientist Staff | Apr 30, 2018 | 1 min read
Meet the family seeking to fund research into a rare disease that afflicts their two boys.