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Building Bridges for Translational Research - A Special Podcast Series
Building Bridges for Translational Research - A Special Podcast Series
Translational scientists discuss their experiences taking preclinical concepts to the market.
Translational scientists discuss their experiences taking preclinical concepts to the market.
Canavan disease
Slow March Toward a Canavan Cure
Ashley Yeager | May 1, 2018 | 5 min read
Two decades after a successful crowdfunding campaign, some clinical trial patients have seen improvements—but there’s still no approved treatment for the disease.
Families of Children with Rare Diseases Fuel Gene Therapy Research
The Scientist Staff | May 1, 2018 | 10+ min read
Crowdfunding can power investigations into diseases that would otherwise receive little attention.
Fighting Canavan Disease
The Scientist Staff | Apr 30, 2018 | 1 min read
Meet the family seeking to fund research into a rare disease that afflicts their two boys.