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Concerns over Efficacy and Cost of Muscle Wasting Treatments
Concerns over Efficacy and Cost of Muscle Wasting Treatments
Two new medications for treating a rare and deadly neuromuscular disease have high prices and questionable efficacies, say scientists.
Concerns over Efficacy and Cost of Muscle Wasting Treatments
Concerns over Efficacy and Cost of Muscle Wasting Treatments

Two new medications for treating a rare and deadly neuromuscular disease have high prices and questionable efficacies, say scientists.

Two new medications for treating a rare and deadly neuromuscular disease have high prices and questionable efficacies, say scientists.

sma

sma spinal muscular atrophy zolgensma in utero fetal gene therapy smn1
Fetal Gene Therapy Helps Mice with Spinal Muscular Atrophy
Alejandra Manjarrez, PhD | Dec 11, 2019 | 4 min read
The animals lived longer and showed milder symptoms than untreated mice, although they didn’t survive as long as wildtype mice.
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