Preliminary Results Point to Success of In Vivo Gene Editing
Preliminary Results Point to Success of In Vivo Gene Editing
Two studies show signs that the introduced DNA is functioning, but it’s too early to know if patients actually benefit.
Preliminary Results Point to Success of In Vivo Gene Editing
Preliminary Results Point to Success of In Vivo Gene Editing

Two studies show signs that the introduced DNA is functioning, but it’s too early to know if patients actually benefit.

Two studies show signs that the introduced DNA is functioning, but it’s too early to know if patients actually benefit.

zinc finger nuclease
Gene Editing Treats Mitochondrial Disorders in Mice
Gene Editing Treats Mitochondrial Disorders in Mice
Catherine Offord | Sep 25, 2018
Researchers used TALENs and zinc finger nucleases to correct disease-causing mutations.
Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging
Kerry Grens | Sep 5, 2018
Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.
Man Receives First In Vivo Gene-Editing Therapy
Man Receives First In Vivo Gene-Editing Therapy
Kerry Grens | Nov 15, 2017
The 44-year-old patient has Hunter syndrome, which doctors hope to treat using zinc finger nucleases.
First In Vivo Human Genome Editing to Be Tested in New Clinical Trial
First In Vivo Human Genome Editing to Be Tested in New Clinical Trial
Abby Olena | May 18, 2017
Sangamo Therapeutics will use zinc finger nucleases to introduce the gene for a missing clotting factor into the livers of men with hemophilia B.
Gene Editing: From Roots to Riches
Gene Editing: From Roots to Riches
Amanda B. Keener | Oct 1, 2016
Advances in genetic manipulation have simplified the once daunting task of rewriting a gene.
Rewritten in Blood
Rewritten in Blood
Ruth Williams | Sep 1, 2014
A modified gene-editing technique corrects mutations in human hematopoietic stem cells.
Positive Developments on the HIV Front
Positive Developments on the HIV Front
Bob Grant | Mar 7, 2014
A gene-editing protocol shows promise, and a second baby who was started on antiretroviral drugs soon after birth appears to be virus-free a year later.
Avant-Garde Science
Mary Beth Aberlin | Jun 1, 2012
Why naked mole-rats and experimental gene therapies remind me of groundbreaking artists.
Messing with HIV
Messing with HIV
Jef Akst | Jun 1, 2012
Sangamo Biosciences is putting a different spin on gene therapy.