Building with sign reading “Novartis”
| 1 min read
No deaths had previously been associated with the muscle-wasting treatment Zolgensma.

zolgensma

Gene Therapy Finds a Fertile Home in Ohio

a baby's hand cradled by an adult hand

Lottery Underway for Rare Muscle-Wasting Disease Gene Therapy

sma spinal muscular atrophy zolgensma in utero fetal gene therapy smn1

Fetal Gene Therapy Helps Mice with Spinal Muscular Atrophy

novartis avexis zolgensma gene therapy fda manipulated data

Leaders of AveXis Out Over Doctored Gene Therapy Data

gene therapy approval used manipulated data

Some Data Backing Novartis Gene-Therapy Approval Manipulated: FDA

FDA Approves Gene Therapy for Spinal Muscular Atrophy

Trending

Photo of John Calhoun crouches within his rodent utopia-turned-dystopia

Universe 25 Experiment

A woman eating chocolate.

Why Do Some Women Crave Chocolate Before Their Period?

An MRI image of a human brain, with a glowing red section which indicates a tumor.

Why Are Breast Cancers That Metastasize to the Brain Hard to Treat?

An anatomical drawing of the placenta showing vascularization and the umbilical cord.

How Can the Placenta Help Us Understand Cancer?

Multimedia

Graphic of silver and gold 3D spheres levitating in space

Transform Omics Workflows with Scalable Cell Prep

LevitasBio
Conceptual image of genomic analysis showing multicolored DNA base sequences depicted as the letters C, G, A, and T.

Accelerating Cancer Research Through Comprehensive Genomic Analysis

Oxford Nanopore Technologies Logo
May digest 2025 cover
May 2025, Issue 1

Study Confirms Safety of Genetically Modified T Cells

A long-term study of nearly 800 patients demonstrated a strong safety profile for T cells engineered with viral vectors.

View this Issue
iStock

TaqMan Probe & Assays: Unveil What's Possible Together

Thermo Fisher Logo
Meet Aunty and Tackle Protein Stability Questions in Research and Development

Meet Aunty and Tackle Protein Stability Questions in Research and Development

Unchained Labs
Detecting Residual Cell Line-Derived DNA with Droplet Digital PCR

Detecting Residual Cell Line-Derived DNA with Droplet Digital PCR

Bio-Rad
How technology makes PCR instruments easier to use.

Making Real-Time PCR More Straightforward

Thermo Fisher Logo

Products

fujirebio-square-logo

Fujirebio Receives Marketing Clearance for Lumipulse® G pTau 217/ β-Amyloid 1-42 Plasma Ratio In-Vitro Diagnostic Test

The Scientist Placeholder Image

Biotium Launches New Phalloidin Conjugates with Extended F-actin Staining Stability for Greater Imaging Flexibility

Leica Microsystems Logo

Latest AI software simplifies image analysis and speeds up insights for scientists

BioSkryb Genomics Logo

BioSkryb Genomics and Tecan introduce a single-cell multiomics workflow for sequencing-ready libraries in under ten hours