Gene Therapy Finds a Fertile Home in Ohio
Gene Therapy Finds a Fertile Home in Ohio
The midwestern state has quietly laid the groundwork for a biotech hub.
Gene Therapy Finds a Fertile Home in Ohio
Gene Therapy Finds a Fertile Home in Ohio

The midwestern state has quietly laid the groundwork for a biotech hub.

The midwestern state has quietly laid the groundwork for a biotech hub.

pharma & biotech
Lottery Underway for Rare Muscle-Wasting Disease Gene Therapy
Lottery Underway for Rare Muscle-Wasting Disease Gene Therapy
Lisa Winter | Jan 7, 2020
The announcement by Novartis, the maker of Zolgensma, has drawn mixed reactions from the spinal muscular atrophy community.
FDA Approves Previously Rejected Muscular Dystrophy Treatment
FDA Approves Previously Rejected Muscular Dystrophy Treatment
Emily Makowski | Dec 13, 2019
The drug Vyondys 53 has met a surrogate endpoint of protein production, but there’s no clear proof it has a clinical benefit.
Biogen Presents Data on Efficacy of Alzheimer’s Drug
Biogen Presents Data on Efficacy of Alzheimer’s Drug
Shawna Williams | Dec 6, 2019
The company and its partner halted two clinical trials for futility early this year, but now say they’ll seek approval for aducanumab.
Monthly Contraceptive Pill Shows Promise in Pig Study
Monthly Contraceptive Pill Shows Promise in Pig Study
Catherine Offord | Dec 5, 2019
A device that releases synthetic hormones slowly over time could one day provide a more practical alternative to daily birth control pills, say scientists.
Former FDA Commissioner Frank Young Dies
Former FDA Commissioner Frank Young Dies
Jef Akst | Dec 2, 2019
The physician-researcher laid the groundwork for genetic cloning and led the US Food and Drug Administration as the country faced the AIDS crisis in the 1980s.
Novartis’s $9.7 Billion Purchase Includes Novel PCSK9 Inhibitor
Novartis’s $9.7 Billion Purchase Includes Novel PCSK9 Inhibitor
Emily Makowski | Nov 25, 2019
The pharmaceutical firm is buying The Medicines Company, which recently devoted its efforts into developing the cholesterol-lowering medication.
Financial Aid Recipients Breaking Funding Rules: Investigation
Financial Aid Recipients Breaking Funding Rules: Investigation
Catherine Offord | Nov 22, 2019
Many early-career clinical scientists receiving support through the NIH’s Loan Repayment Program have accepted disallowed industry funding, Science reveals.
Trial of Gene Therapy for Duchenne Muscular Dystrophy Put on Hold
Trial of Gene Therapy for Duchenne Muscular Dystrophy Put on Hold
Catherine Offord | Nov 12, 2019
The US Food and Drug Administration halts a study by Solid Biosciences after a patient experiences severe side effects following treatment.
China Approves Alzheimer’s Treatment that Targets the Microbiome
China Approves Alzheimer’s Treatment that Targets the Microbiome
Kerry Grens | Nov 5, 2019
Oligomannate, derived from a compound in seaweed, suppresses neural inflammation caused by gut bacteria in mice.