Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging
Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.
Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging

Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.

Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.

clinical research
Early Results of First In Vivo Gene-Editing Trial Encouraging
Early Results of First In Vivo Gene-Editing Trial Encouraging
Kerry Grens | Sep 5, 2018
Two patients who received Sangamo’s zinc finger–based treatment for Hunter syndrome have lower biomarkers of the condition, but no signs of new enzyme production.
Adult Cardiac Stem Cells Don’t Exist: Study
Adult Cardiac Stem Cells Don’t Exist: Study
Diana Kwon | Sep 5, 2018
A mouse study adds to the growing body of work disputing the ability of progenitor cells to regenerate muscle tissue in adult mammals’ hearts.
Vibrations Restore Sense of Movement in Prosthetics
Vibrations Restore Sense of Movement in Prosthetics
Diana Kwon | Sep 1, 2018
Scientists recreate proprioception for people with artificial arms using a perceptual illusion.
First iPS Cell Trial for Heart Disease Raises Excitement, Concern
First iPS Cell Trial for Heart Disease Raises Excitement, Concern
Katarina Zimmer | Aug 31, 2018
Without knowing the cells’ mechanism of action, researchers question the best way to administer them to patients.
Cell and Gene Therapy Tracker: Global CAR T-Cell Trials
Cell and Gene Therapy Tracker: Global CAR T-Cell Trials
The Scientist Staff | Aug 22, 2018
Investigators have launched numerous clinical trials that test the efficacy of the immunotherapy. Here is a global accounting of these experiments.
Dartmouth Professor Plagiarized His Colleague, University Says
Dartmouth Professor Plagiarized His Colleague, University Says
Jef Akst | Aug 20, 2018
H. Gilbert Welch, a health policy expert who has advocated against superfluous cancer screening, published another Dartmouth researcher’s work, according to the university administration.
Synthetic Bacteria Help Treat Phenylketonuria in MiceSynthetic Bacteria Help Treat Phenylketonuria in Mice
Synthetic Bacteria Help Treat Phenylketonuria in Mice
Diana Kwon | Aug 17, 2018
The genetically engineered probiotic, already in clinical trials, may ease patients’ strict dietary regimes.
Drug Approval Could Boost Research on Marijuana Treatment for Autism
Drug Approval Could Boost Research on Marijuana Treatment for Autism
Jessica Wright | Aug 17, 2018
Epidiolex, a cannabis-derived medicine for epilepsy, will prompt federal regulatory changes that could crack open access to study the plant.
The NIH Loosens Grip on Gene Therapy Trials
The NIH Loosens Grip on Gene Therapy Trials
Kerry Grens | Aug 16, 2018
The agency proposes ceding its scrutiny of these studies to the FDA.
Q&A: Anthony Fauci Describes an Experimental Ebola Treatment
Q&A: Anthony Fauci Describes an Experimental Ebola Treatment
Shawna Williams | Aug 14, 2018
The monoclonal antibody, known as mAb114, is likely to be used in the current Ebola outbreak in DRC.