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| 9 min read
New precision genome editing technologies are transforming the therapeutic landscape for patients with certain cancers and genetic diseases.

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Catch Me If You Can: Sequencing Screens for Rare Disease Genes

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The heart sections on the left present defects while the hearts on the right do not show defects. 

Genetic Signatures of a Defective Heart

Keeping Kidneys Healthy with a Hand from AI

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Defending against Dravet

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The Future of Gene Therapy for a Rare Pediatric Autoimmune Disease

Researchers in George Church&rsquo;s lab modified wild type ADK proteins (left) in <em >E.coli</em>, furnishing them with an nonstandard amino acid (nsAA) meant to biocontain the resulting bacterial strain.

A Pioneer of The Multiplex Frontier

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Building Bridges for Translational Research - A Special Podcast Series

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Doctors Treat a Rare Genetic Condition Before Patient Is Born

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Scans of Sundry Variant Types Uncover Autism-Linked Genes

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Deficient RNA Editing Implicated in Inflammatory Disease 

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Q&A: Whole Genomes of 150,000 Britons Reveal Novel Genetic Variants

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Physician and Geneticist Leon Rosenberg Dies at 89

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First Person Dosed in Novel Gene Editing Clinical Trial

&nbsp;Learn how genetics research identifies new targets for complex disease therapies.

Revealing Gene Functions in Health and Disease

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Genetic Mutations Can Be Benign or Cancerous—a New Method to Differentiate Between Them Could Lead to Better Treatments

Optimize quality control in gene therapy viral vector production

Empty or Full: Separating Therapeutically Viable Viral Vectors

An orange CRISPR Cas 9 enzyme cutting DNA

CRISPR-Based Treatment Successfully Lowers Toxic Protein Levels

PATH TO TREATMENT: Marley, pictured here with her father, was diagnosed with the rare genetic condition Bachmann-Bupp syndrome a few years ago.

Doctors Treat Girl’s Genetic Disorder with Repurposed Drug

Man with glasses wearing yellow long sleeve shirt sits at a desk, surrounded by stacks of paper

Stephen Warren, Icon of Fragile X Research, Dies at 67

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Antisense Oligonucleotides Cross Rodents’ Blood-Brain Barrier

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Universe 25 Experiment

Large clumps of bacteria (pink) entrapped by webs of DNA (green) released by neutrophils in human urine.

When a Urinary Tract Infection Strikes, What Protects the Kidneys?

A white dire wolf stands in a grassy enclosure in front of a pile of logs.

Dire Wolf De-Extinction Debate Divides Scientists

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ALS Disturbs Sleep Prior to Symptom Onset

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Conceptual image of biochemical laboratory sample preparation showing glassware and chemical formulas in the foreground and a scientist holding a pipette in the background.

Taking the Guesswork Out of Quality Control Standards

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Green Cooling

Thermo Scientific™ Centrifuges with GreenCool Technology

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April 1, 2025, Issue 1

Bunsen Burners and Bad Hair Days

Lab safety rules dictate that one must tie back long hair. Rosemarie Hansen learned the hard way when an open flame turned her locks into a lesson.

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Conceptual image of biochemical laboratory sample preparation showing glassware and chemical formulas in the foreground and a scientist holding a pipette in the background.

Taking the Guesswork Out of Quality Control Standards

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An illustration of PFAS bubbles in front of a blue sky with clouds.

PFAS: The Forever Chemicals

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Unlocking the Unattainable in Gene Construction

Unlocking the Unattainable in Gene Construction

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Comparing Analytical Solutions for High-Throughput Drug Discovery

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Thermo Scientific™ Centrifuges with GreenCool Technology

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Singleron Biotechnologies and Hamilton Bonaduz AG Announce the Launch of Tensor to Advance Single Cell Sequencing Automation

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Zymo Research Launches Research Grant to Empower Mapping the RNome

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Cytosurge Appoints Magid Haddouchi as Chief Commercial Officer