Positive Trial Results for Experimental DMD Gene Therapy
Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.
Positive Trial Results for Experimental DMD Gene Therapy
Positive Trial Results for Experimental DMD Gene Therapy

Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.

Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.

Muscular Dystrophy
Nonviral CRISPR Delivery a Success
Nonviral CRISPR Delivery a Success
Abby Olena | Oct 2, 2017
Researchers use gold nanoparticles to deliver CRISPR-Cas9 and correct a point mutation in a mouse model of Duchenne muscular dystrophy. 
Dogs with Duchenne Treated with Gene Therapy
Dogs with Duchenne Treated with Gene Therapy
Diana Kwon | Jul 25, 2017
Researchers restored muscle function in animals with muscular dystrophy.
CRISPR Restores Muscle Function in Mice
CRISPR Restores Muscle Function in Mice
Diana Kwon | Jul 17, 2017
Scientists use the gene-editing tool to treat animals with a rare form of congenital muscular dystrophy.