From new treatments to an investigation into the virus’s origins, here are some of the developments we can expect this year.

The world was rocked by the COVID-19 pandemic this year, but researchers rose to all manner of challenges.

It’s not clear why the patients with Leber hereditary optic neuropathy, a mitochondrial disorder that causes blindness, also experienced the modest benefits in their untreated eye.

The Past, Present, and Future of Gene Therapy: How to Scale-up Successfully

The third FDA approval of an RNAi-based therapeutic marks the growing success of a technique that took two decades to get off the ground.

As COVID-19 therapies get emergency-use green lights, the Biden administration must organize a therapeutic review board to help identify what’s working and what’s not.

Long before Moderna’s and Pfizer’s COVID-19 shots, scientists had been considering the use of genetically encoded vaccines in the fight against infectious diseases, cancer, and more.

The results mark the second experimental COVID-19 vaccine to show high efficacy, but the study is not complete and the data have not been peer reviewed.

Scientists uncover the promise of mesenchymal stem cells (MSCs), also known as medicinal signaling cells, to modulate the immune system and regenerate tissue.