The NIH Loosens Grip on Gene Therapy Trials
The NIH Loosens Grip on Gene Therapy Trials
The agency proposes ceding its scrutiny of these studies to the FDA.
The NIH Loosens Grip on Gene Therapy Trials
The NIH Loosens Grip on Gene Therapy Trials

The agency proposes ceding its scrutiny of these studies to the FDA.

The agency proposes ceding its scrutiny of these studies to the FDA.

clinical trials
Drug Approval Could Boost Research on Marijuana Treatment for Autism
Drug Approval Could Boost Research on Marijuana Treatment for Autism
Jessica Wright | Aug 17, 2018
Epidiolex, a cannabis-derived medicine for epilepsy, will prompt federal regulatory changes that could crack open access to study the plant.
FDA Approves Oral Drug for Fabry Disease
FDA Approves Oral Drug for Fabry Disease
Ashley Yeager | Aug 13, 2018
The medicine increases the activity of a deficient enzyme in certain patients with the condition.
Opinion: Learning from Immunotherapy’s Recent Failures
Opinion: Learning from Immunotherapy’s Recent Failures
Luis Felipe Campesato | Aug 1, 2018
The promise of immunotherapy is real. We now need to figure out how to maximize the number of patients the approach benefits.
Trial Launched to Treat Parkinson’s with Reprogrammed Stem Cells
Trial Launched to Treat Parkinson’s with Reprogrammed Stem Cells
Diana Kwon | Jul 31, 2018
Surgeons will inject approximately 5 million dopamine-producing progenitor cells into patients’ brains.
Ultrasound Opens Blood-Brain Barrier in Alzheimer’s Patients
Ultrasound Opens Blood-Brain Barrier in Alzheimer’s Patients
Ashley Yeager | Jul 26, 2018
A Phase 1 clinical trial shows the noninvasive technique is safe and could aid in the delivery treatments to the brain.
Gene Editing Reduces Monkeys’ Cholesterol
Gene Editing Reduces Monkeys’ Cholesterol
Ashley Yeager | Jul 10, 2018
The results could lead to a treatment to lower cholesterol in patients with hypercholesterolemia.
Canada Could Come to the Fore in Cannabis Research
Canada Could Come to the Fore in Cannabis Research
Ashley Yeager | Jul 6, 2018
The coming legalization of recreational marijuana is already increasing funding for studies, but regulations on such research have been slow to change.
Cardiac Cell Transplants Help Monkeys’ Hearts
Cardiac Cell Transplants Help Monkeys’ Hearts
Ashley Yeager | Jul 2, 2018
The organ’s blood-pumping capacity improved with the infusion of cells, a study shows.
Poliovirus Therapy May Extend Lives of Advanced Brain-Cancer Patients
Poliovirus Therapy May Extend Lives of Advanced Brain-Cancer Patients
Ashley Yeager | Jun 26, 2018
More than one-fifth of individuals treated with the genetically modified virus survived at least three years.