FDA Approves Gene Therapy for Spinal Muscular Atrophy
FDA Approves Gene Therapy for Spinal Muscular Atrophy
At $2 million for a single dose, Novartis’s Zolgensma is the most expensive medicine to date, but still less expensive over a lifetime than another approved drug for the rare genetic disease.
FDA Approves Gene Therapy for Spinal Muscular Atrophy
FDA Approves Gene Therapy for Spinal Muscular Atrophy

At $2 million for a single dose, Novartis’s Zolgensma is the most expensive medicine to date, but still less expensive over a lifetime than another approved drug for the rare genetic disease.

At $2 million for a single dose, Novartis’s Zolgensma is the most expensive medicine to date, but still less expensive over a lifetime than another approved drug for the rare genetic disease.

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Image of the Day: High Contrast
Image of the Day: High Contrast
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Of the Hemiptera bugs, milkweed-chomping Oncopeltus fasciatus have hung onto more smell and taste receptors than their liquid-guzzling relatives.
Image of the Day: Neuron Guides
Image of the Day: Neuron Guides
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A gene helps motor neurons successfully venture out from the spinal cord to muscles during mouse development.
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Image of the Day: Life and Death
Image of the Day: Life and Death
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Image of the Day: Dystrophin Restored
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CRISPRed heart muscle cells from humans gain the ability to make a protein missing in Duchenne muscular dystrophy.
Barbara Low, Trailblazing Woman in X-Ray Crystallography, Dies
Barbara Low, Trailblazing Woman in X-Ray Crystallography, Dies
Carolyn Wilke | Mar 15, 2019
The former Columbia University professor’s early work helped illuminate the structure of penicillin, allowing chemists to make variants and broaden the scope of antibiotic treatments.
Image of the Day: Taken to Heart
Image of the Day: Taken to Heart
Carolyn Wilke | Mar 14, 2019
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Gum Disease Could Drive Alzheimer’s: Study
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Image of the Day: Sentinel Cells
Image of the Day: Sentinel Cells
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Researchers hacked the genetic machinery of E. coli to make them glow and identify proteins linked to cancer.