Severe Toxicity Reported in High-Dose AAV Gene Therapy in Animals
Jim Daley | Jan 31, 2018
Biotech stocks fell in response to the news.
WIKIMEDIA, DR EDWIN P EWING JR
Positive Trial Results for Experimental DMD Gene Therapy
Positive Trial Results for Experimental DMD Gene Therapy
Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.
Preliminary data from Sarepta Therapeutics has exceeded expectations, causing a surge in company stock prices this week.
Gene Therapy Temporarily Reverses Type 1 Diabetes in Mice
Shawna Williams | Jan 4, 2018
Pancreatic cells engineered to produce insulin did not immediately provoke an immune response.
Ancient Viruses as Gene Therapy Vectors
Ashley P. Taylor | Jul 31, 2015
Researchers deploy ancestors of today’s adeno-associated viruses to deliver gene therapies without immune system interference.
Reducing Gene Therapy-Related Risk
Kerry Grens | Jan 22, 2015
In a mouse model of a rare disease, scientists have figured out how to reduce the elevated cancer risk tied to a gene therapy treatment.
Gene Therapy Arrives in Europe
Sabrina Richards | Nov 6, 2012
The European Commission approves the Western hemisphere’s first gene therapy, aimed at correcting a lipid-processing disorder.